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Orchard Therapeutics

Orchard Therapeutics is a biotechnology company dedicated to bringing transformative gene therapies to patients with serious and life-threatening orphan diseases

Orchard Therapeutics is a spin-out from the Institute of Child Health (ICH) at UCL, commercialising a gene therapy platform with the potential to cure a range of rare childhood genetic disorders in a single treatment. The company’s programmes use the potential of ex-vivo autologous haematopoietic stem cell gene therapies to restore normal gene function in severe and life-threatening inherited disorders, including immunodeficiencies and a range of neurological disorders, and have demonstrated excellent safety and efficacy in ongoing clinical trials. Orchard’s shareholders include F-Prime Ventures, UCLB and the UCL Technology Fund.